“At this moment, my son is a perfect ice sculpture of himself. And he is slowly melting away. That’s what happens, these boys just kind of melt away.”
What is DMD?
“I try to live a normal life. As much as I can. If you are motivated to do something, you live longer.”
Debiopharm International SA and Solid Biosciences, LLC, announce a collaboration to explore the use of Alisporivir (Debio 025) in muscular dystrophy.
To advance the development of its gene therapy platform for Duchenne muscular dystrophy.
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