July 27, 2017
Cambridge, Ma

Publication: Gene Transfer Corrects Severe Muscle Defects in Mice with Duchenne Muscular Dystrophy

Results from a study led by Dr. Dongsheng Duan of the University of Missouri showed that AAV-mediated microdystrophin gene transfer effectively restored muscle strength in a severe mouse model of Duchenne muscular dystrophy (DMD). These findings further support the initiation of clinical trials for SGT-001. 

Read the full publication here.

Related news

Jun26

Ilan Ganot, Co-Founder and CEO, Assumes Additional Role of President
Gilad Hayeem, Co-Founder, President and Board Member, Retires to Pursue Other Activities

Jun18

We’re pleased to share with you that the FDA has lifted the clinical hold on IGNITE DMD.

Jun18

- Activities to Resume Enrollment in IGNITE DMD Phase I/II Clinical Trial are Underway

- Conference Call Scheduled for Today at 8:30 A.M. ET

May19

- Data Reinforce Potential of SGT-001 as an Important Treatment Candidate for DMD -

- Company Continues to Advance Gene Therapy Portfolio -

May10
Company Finalizing Response to FDA Regarding Clinical Hold on SGT-001 Phase I/II Clinical Trial
Apr18

- Full Clinical Hold Letter from the FDA Received; Company to Respond in the Coming Weeks -

- Manufacturing-related Partial Clinical Hold on the High Dose of SGT-001 Resolved -

Mar29

Solid Biosciences Inc. (NASDAQ:SLDB) today reported financial results for the full year ended December 31, 2017 and provided a corporate update.

Mar14

Solid Biosciences Inc. (NASDAQ:SLDB) today announced it has received notification from the U.S. Food and Drug Administration ( FDA ) that IGNITE DMD, its Phase I/II clinical trial for SGT-001 microdystrophin gene transfer in Duchenne muscular dystrophy (DMD), has been placed on Clinical Hold.

Feb28

Solid Biosciences is proud to join the global rare disease community again this year to observe Rare Disease Day

Nov30

Phase I/II adaptive clinical trial to evaluate safety and efficacy in ambulatory and non-ambulatory children and adolescents.

Pages

More information about Solid?

Please subscribe to receive our latest news